PANEL: How to lay the groundwork for a successful rare disease trial through early patient engagement

  • Working closely with patients, caregivers and advocacy groups in clinical trial design
  • The importance of building a close relationship with patients for trials where patients are the expert in their disease
  • Reducing the financial burden of clinical trial participation on patients
  • How to make trial participation easier on patients: where are the main hurdles impacting enrolment?
  • Building long term relationships with patients post clinical trials