Archives: Agenda

• Country & site selection
• Patient identification & recruitment
• Timelines & startup complexity
• Consultants & collaboration
• Conferences & knowledge sharing

• Reviewing challenges in designing a rare disease trial
• Discussing approaches to optimize a rare disease clinical trial design
• Considering incorporating a competitive mindset in designing a rare disease clinical trial

Interactive roundtable sessions offer a unique opportunity to come together with your peers to share best practice and develop solutions to critical challenges facing the industry as a whole. Each discussion will be led by a table moderator and will focus on a different challenge within rare disease clinical trials.

Roundtables are an exciting, interactive way to build your personal network and learn from the experience and expertise of others. After 45 minutes, delegates will have the opportunity to swap and choose a different table, and each roundtable will run twice.

Roundtable 1: Sharing experiences and highlighting importance of decentralizing in rare disease trials

Leila Cupersmith, Rare Disease Clinical Trial Expert & Patient Advocacy

Roundtable 2: Overcoming patient retention challenges in rare disease trials

Jenifer Waldrop, Executive Director, Rare Disease Diversity Coalition

Roundtable 3: Using new technologies in rare disease trials

Bruce Bloom, Chief Collaboration Officer, Healx

• Deciding the right level of oversight: key considerations
• Addressing communication hurdles and how to overcome them
• Supporting sites for operational improvement and inspection readiness